But to their knowledge, this is the first study that has tested gene therapy on a heart disease model in non-human primates. The team also believes that this approach may be particularly effective for ...

Researchers have shown that they can help the heart to normalize strength and rhythm following a heart attack by delivering ...

As gene therapy continues to change, so must the federal framework set up to oversee it. As new biotechnologies continue to emerge, the NIH and the FDA are proposing reductions in duplicative overs ...

‘Groundbreaking’ Gene-Editing Therapy Receives Ethical Thumbs Up Casgevy is a new treatment for sickle cell disease, a blood disorder that affects approximately 100,000 Americans.

Researchers from Drexel University’s College of Arts and Sciences and College of Medicine have found a potential new ...

Bacterial ‘Nanosyringe’ Could Deliver Gene Therapy to Human Cells This novel injection system could help advance gene therapy by nimbly inserting gene-editing enzymes into a variety of cell types ...

Besides addressing lingering safety concerns, gene therapy is exploring applications beyond the correction of single-gene mutations. Possibilities include polygenic and gene-independent approaches.

The post Gene-Therapy Treatment Of Infant With Rare Genetic Condition Successful In World First first on TwistedSifter.

The field of gene therapy has evolved through several stages, from its origins in molecular biology, to virus-mediated transfer of foreign genetic material, to the rapid ascent of early human ...

The gene editor will be used in lab dishes in cancer and blood disorder trials, and to directly edit a gene in human eyes in a blindness therapy test.